Hunting for a cure: the therapeutic potential of gene therapy in Duchenne muscular dystrophy

• Main Authors: Hashim, Hasnur Zaman, Che Abdullah, Shahrin Tarmizi, Wan Sulaiman, Wan Aliaa, Fan, Kee Hoo, Basri, Hamidon
• Format: Article
• Language: English; English; English
• Published: Elsevier 2014
• Subjects: RC0321 Neuroscience. Biological psychiatry. Neuropsychiatry
• Online Access: http://irep.iium.edu.my/36244/1/hunting_for_cure.pdf; http://irep.iium.edu.my/36244/4/scopus.pdf; http://irep.iium.edu.my/36244/5/Hunting_for_a_cure_The_therapeutic_potential_of_gene_therapy_in.pdf; http://irep.iium.edu.my/36244/; http://www.sciencedirect.com/science/article/pii/S101631901400007X#

Duchenne muscular dystrophy (DMD) is an incurable disease and the search for a cure is a challenging journey. However, with recent encouraging progress, we are seeing a light at the end of a long tunnel. This review focuses on several main strategies in gene therapy, including truncated dystrophin g...